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DCRT Dutch Center for RNA Therapeutics

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About

DCRT Dutch Center for RNA Therapeutics. DCRT focusses on splice modulation for patients with unique, eligibile mutations. This is achieved with antisense oligonucleotides, small stretches of chemically modified RNA. In exon skipping, pre-mRNA splicing is modulated such that an exon is skipped.

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Websiternatherapy.nl ↗
Site languageEnglish
Last read1 Oct 2026
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